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CAS NO: 1173755-55-9
Cov mis mos molecular: C364H569N177O122P30
Molecular Luj: 10305.74
EINECS NO: N / A
MDL NO: N/A
Product Description:
Khoom npe: Eteplirsen CAS 1173755-55-9
Synonyms:
(P-deoxy-P-(dimethylamino))(2',3'-dideoxy-2',3'-imino-2',3'-seco)(2'a->5')(C-m5U-CCAACA-m5U-CAAGGAAGA-m5U-GGCA-m5U-m5U-m5U-C-m5U-AG),5'-(P-(4-((2-) (2-(2-hydroxyethoxy)ethoxy)ethoxy)carbonyl)-1-piperazinyl)-N,N-dimethylphosphonamidate) RNA;
Chemical & Physical Properties:
Cov tsos mob: dawb mus rau cov hmoov dawb dawb
Assay: Ntau dua lossis sib npaug rau 99.0%
Eteplirsen, tseem hu ua AVI-4658, yog ib qho kev sim tshuaj, tam sim no hauv kev sim tshuaj. Nws yog tsim los rau kev kho mob, tab sis tsis yog kev kho, ntawm qee qhov kev hloov pauv uas ua rau Duchenne muscular dystrophy (DMD), cov kab mob caj ces degenerative leeg. Eteplirsen yog cov khoom lag luam ntawm Sarepta Therapeutics Inc. Eteplirsen tsuas yog lub hom phiaj kev hloov pauv hauv cheeb tsam cuam tshuam hauv 13% ntawm DMD cov neeg mob.
Yog tias koj txaus siab rau peb cov khoom lossis muaj lus nug, thov koj xav tiv tauj peb!
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Cim npe nrov: eteplirsen cas 1173755-55-9, manufacturers, lwm tus neeg, Hoobkas, yuav, Tshuag