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APIs thiab Intermediates
Eteplirsen CAS 1173755-55-9

Eteplirsen CAS 1173755-55-9

CAS NO: 1173755-55-9
Cov mis mos molecular: C364H569N177O122P30
Molecular Luj: 10305.74
EINECS NO: N / A
MDL NO: N/A

Txhawb tshuaj

Product Description:

Khoom npe: Eteplirsen CAS 1173755-55-9

 

Synonyms:

(P-deoxy-P-(dimethylamino))(2',3'-dideoxy-2',3'-imino-2',3'-seco)(2'a->5')(C-m5U-CCAACA-m5U-CAAGGAAGA-m5U-GGCA-m5U-m5U-m5U-C-m5U-AG),5'-(P-(4-((2-) (2-(2-hydroxyethoxy)ethoxy)ethoxy)carbonyl)-1-piperazinyl)-N,N-dimethylphosphonamidate) RNA;

 

Chemical & Physical Properties:

Cov tsos mob: dawb mus rau cov hmoov dawb dawb

Assay: Ntau dua lossis sib npaug rau 99.0%

 

Eteplirsen, tseem hu ua AVI-4658, yog ib qho kev sim tshuaj, tam sim no hauv kev sim tshuaj. Nws yog tsim los rau kev kho mob, tab sis tsis yog kev kho, ntawm qee qhov kev hloov pauv uas ua rau Duchenne muscular dystrophy (DMD), cov kab mob caj ces degenerative leeg. Eteplirsen yog cov khoom lag luam ntawm Sarepta Therapeutics Inc. Eteplirsen tsuas yog lub hom phiaj kev hloov pauv hauv cheeb tsam cuam tshuam hauv 13% ntawm DMD cov neeg mob.

 

Yog tias koj txaus siab rau peb cov khoom lossis muaj lus nug, thov koj xav tiv tauj peb!

 

Cov khoom raws li patent yog muab rau R & D lub hom phiaj nkaus xwb. Txawm li cas los xij, lub luag haujlwm kawg tsuas yog nrog tus neeg yuav khoom.

Cim npe nrov: eteplirsen cas 1173755-55-9, manufacturers, lwm tus neeg, Hoobkas, yuav, Tshuag

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